Safety and efficacy of risdiplam in patients with type 1 spinal muscular atrophy (FIREFISH part 2): secondary analyses from an open-label trial

Giovanni Baranello; Eugenio Maria Mercuri; Giorgia Coratti; Marika Pane; Concetta Palermo; Maria Carmela Pera; Giulia Maria Amorelli; Guglielmo D'Amico; Lorenzo Orazi; Giorgia Coratti; Daniela Leone; Laura Antonaci; Roberto De Sanctis

doi:10.1016/S1474-4422(22)00339-8

Safety and efficacy of risdiplam in patients with type 1 spinal muscular atrophy (FIREFISH part 2): secondary analyses from an open-label trial

Giovanni Baranello, Eugenio Maria Mercuri, Giorgia Coratti, Marika Pane, Concetta Palermo, Maria Carmela Pera, Giulia Maria Amorelli, Guglielmo D'Amico, Lorenzo Orazi, Giorgia Coratti, Daniela Leone, Laura Antonaci, Roberto De Sanctis

Risultato della ricerca: Contributo in rivista › Articolo

Lingua originale	Inglese
pagine (da-a)	1110-1119
Numero di pagine	10
Rivista	LANCET NEUROLOGY
Volume	21
DOI	https://doi.org/10.1016/S1474-4422(22)00339-8
Stato di pubblicazione	Pubblicato - 2022

Keywords

spinal muscular atrophy

Accesso al documento

10.1016/S1474-4422(22)00339-8

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Cita questo

Baranello, G., Mercuri, E. M., Coratti, G., Pane, M., Palermo, C., Pera, M. C., Amorelli, G. M., D'Amico, G., Orazi, L., Coratti, G., Leone, D., Antonaci, L., & De Sanctis, R. (2022). Safety and efficacy of risdiplam in patients with type 1 spinal muscular atrophy (FIREFISH part 2): secondary analyses from an open-label trial. LANCET NEUROLOGY, 21, 1110-1119. https://doi.org/10.1016/S1474-4422(22)00339-8

@article{c30b96d1b03e410aba6063d872594718,

title = "Safety and efficacy of risdiplam in patients with type 1 spinal muscular atrophy (FIREFISH part 2): secondary analyses from an open-label trial",

keywords = "spinal muscular atrophy, spinal muscular atrophy",

author = "Giovanni Baranello and Mercuri, {Eugenio Maria} and Giorgia Coratti and Marika Pane and Concetta Palermo and Pera, {Maria Carmela} and Amorelli, {Giulia Maria} and Guglielmo D'Amico and Lorenzo Orazi and Giorgia Coratti and Daniela Leone and Laura Antonaci and {De Sanctis}, Roberto",

year = "2022",

doi = "10.1016/S1474-4422(22)00339-8",

language = "English",

volume = "21",

pages = "1110--1119",

journal = "LANCET NEUROLOGY",

issn = "1474-4422",

publisher = "Lancet Publishing Group",

}

Baranello, G, Mercuri, EM , Coratti, G , Pane, M, Palermo, C, Pera, MC, Amorelli, GM, D'Amico, G, Orazi, L, Coratti, G, Leone, D, Antonaci, L & De Sanctis, R 2022, 'Safety and efficacy of risdiplam in patients with type 1 spinal muscular atrophy (FIREFISH part 2): secondary analyses from an open-label trial', LANCET NEUROLOGY, vol. 21, pagg. 1110-1119. https://doi.org/10.1016/S1474-4422(22)00339-8

TY - JOUR

T1 - Safety and efficacy of risdiplam in patients with type 1 spinal muscular atrophy (FIREFISH part 2): secondary analyses from an open-label trial

AU - Baranello, Giovanni

AU - Mercuri, Eugenio Maria

AU - Coratti, Giorgia

AU - Pane, Marika

AU - Palermo, Concetta

AU - Pera, Maria Carmela

AU - Amorelli, Giulia Maria

AU - D'Amico, Guglielmo

AU - Orazi, Lorenzo

AU - Coratti, Giorgia

AU - Leone, Daniela

AU - Antonaci, Laura

AU - De Sanctis, Roberto

PY - 2022

Y1 - 2022

KW - spinal muscular atrophy

UR - http://hdl.handle.net/10807/226647

U2 - 10.1016/S1474-4422(22)00339-8

DO - 10.1016/S1474-4422(22)00339-8

M3 - Article

SN - 1474-4422

VL - 21

SP - 1110

EP - 1119

JO - LANCET NEUROLOGY

JF - LANCET NEUROLOGY

ER -