Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

Eugenio Maria Mercuri; Juan J Vilchez; Odile Boespflug-Tanguy; Craig M Zaidman; Jean K Mah; Nathalie Goemans; Wolfgang Müller-Felber; Erik H Niks; Ulrike Schara-Schmidt; Enrico Bertini; Giacomo P Comi; Katherine D Mathews; Laurent Servais; Krista Vandenborne; Jessika Johannsen; Sonia Messina; Stefan Spinty; Laura Mcadam; Kathryn Selby; Barry Byrne; Chamindra G Laverty; Kevin Carroll; Giulia Zardi; Sara Cazzaniga; Nicoletta Coceani; Paolo Bettica; Craig M Mcdonald

doi:10.1016/S1474-4422(24)00036-X

Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

Eugenio Maria Mercuri, Juan J Vilchez, Odile Boespflug-Tanguy, Craig M Zaidman, Jean K Mah, Nathalie Goemans, Wolfgang Müller-Felber, Erik H Niks, Ulrike Schara-Schmidt, Enrico Bertini, Giacomo P Comi, Katherine D Mathews, Laurent Servais, Krista Vandenborne, Jessika Johannsen, Sonia Messina, Stefan Spinty, Laura Mcadam, Kathryn Selby, Barry ByrneChamindra G Laverty, Kevin Carroll, Giulia Zardi, Sara Cazzaniga, Nicoletta Coceani, Paolo Bettica, Craig M Mcdonald

Risultato della ricerca: Contributo in rivista › Articolo in rivista › peer review

Lingua originale	English
pagine (da-a)	393-404
Numero di pagine	12
Rivista	LANCET NEUROLOGY
Volume	23
DOI	https://doi.org/10.1016/S1474-4422(24)00036-X
Stato di pubblicazione	Pubblicato - 2024

Keywords

duchenne muscular dystrophy

Accesso al documento

10.1016/S1474-4422(24)00036-X

Altri file e collegamenti

Link a IRIS PubliCatt

Cita questo

Mercuri, E. M., Vilchez, J. J., Boespflug-Tanguy, O., Zaidman, C. M., Mah, J. K., Goemans, N., Müller-Felber, W., Niks, E. H., Schara-Schmidt, U., Bertini, E., Comi, G. P., Mathews, K. D., Servais, L., Vandenborne, K., Johannsen, J., Messina, S., Spinty, S., Mcadam, L., Selby, K., ... Mcdonald, C. M. (2024). Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial. LANCET NEUROLOGY, 23, 393-404. https://doi.org/10.1016/S1474-4422(24)00036-X

@article{50ff256ff02a474cbc241a91c721bf66,

title = "Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial",

keywords = "duchenne muscular dystrophy, duchenne muscular dystrophy",

author = "Mercuri, {Eugenio Maria} and Vilchez, {Juan J} and Odile Boespflug-Tanguy and Zaidman, {Craig M} and Mah, {Jean K} and Nathalie Goemans and Wolfgang M{\"u}ller-Felber and Niks, {Erik H} and Ulrike Schara-Schmidt and Enrico Bertini and Comi, {Giacomo P} and Mathews, {Katherine D} and Laurent Servais and Krista Vandenborne and Jessika Johannsen and Sonia Messina and Stefan Spinty and Laura Mcadam and Kathryn Selby and Barry Byrne and Laverty, {Chamindra G} and Kevin Carroll and Giulia Zardi and Sara Cazzaniga and Nicoletta Coceani and Paolo Bettica and Mcdonald, {Craig M}",

year = "2024",

doi = "10.1016/S1474-4422(24)00036-X",

language = "English",

volume = "23",

pages = "393--404",

journal = "LANCET NEUROLOGY",

issn = "1474-4422",

publisher = "Lancet Publishing Group",

}

Mercuri, EM, Vilchez, JJ, Boespflug-Tanguy, O, Zaidman, CM, Mah, JK, Goemans, N, Müller-Felber, W, Niks, EH, Schara-Schmidt, U, Bertini, E, Comi, GP, Mathews, KD, Servais, L, Vandenborne, K, Johannsen, J, Messina, S, Spinty, S, Mcadam, L, Selby, K, Byrne, B, Laverty, CG, Carroll, K, Zardi, G, Cazzaniga, S, Coceani, N, Bettica, P & Mcdonald, CM 2024, 'Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial', LANCET NEUROLOGY, vol. 23, pagg. 393-404. https://doi.org/10.1016/S1474-4422(24)00036-X

Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial. / Mercuri, Eugenio Maria; Vilchez, Juan J; Boespflug-Tanguy, Odile et al.
In: LANCET NEUROLOGY, Vol. 23, 2024, pag. 393-404.

Risultato della ricerca: Contributo in rivista › Articolo in rivista › peer review

TY - JOUR

T1 - Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

AU - Mercuri, Eugenio Maria

AU - Vilchez, Juan J

AU - Boespflug-Tanguy, Odile

AU - Zaidman, Craig M

AU - Mah, Jean K

AU - Goemans, Nathalie

AU - Müller-Felber, Wolfgang

AU - Niks, Erik H

AU - Schara-Schmidt, Ulrike

AU - Bertini, Enrico

AU - Comi, Giacomo P

AU - Mathews, Katherine D

AU - Servais, Laurent

AU - Vandenborne, Krista

AU - Johannsen, Jessika

AU - Messina, Sonia

AU - Spinty, Stefan

AU - Mcadam, Laura

AU - Selby, Kathryn

AU - Byrne, Barry

AU - Laverty, Chamindra G

AU - Carroll, Kevin

AU - Zardi, Giulia

AU - Cazzaniga, Sara

AU - Coceani, Nicoletta

AU - Bettica, Paolo

AU - Mcdonald, Craig M

PY - 2024

Y1 - 2024

KW - duchenne muscular dystrophy

UR - http://hdl.handle.net/10807/278121

U2 - 10.1016/S1474-4422(24)00036-X

DO - 10.1016/S1474-4422(24)00036-X

M3 - Article

SN - 1474-4422

VL - 23

SP - 393

EP - 404

JO - LANCET NEUROLOGY

JF - LANCET NEUROLOGY

ER -