@article{7e5716dc9d8a448caf212257b4a56009,
title = "Randomized, double-blind, placebo-controlled trial of phenylbutyrate in spinal muscular atrophy.",
keywords = "phenykbutyrate, spinal muscular atrophy, phenykbutyrate, spinal muscular atrophy",
author = "Mercuri, \{Eugenio Maria\} and Carla Angelozzi and Giovanni Neri and Tiziano, \{Francesco Danilo\} and Brahe, \{Cristina Beate\}",
year = "2007",
language = "English",
pages = "51--55",
journal = "Neurology",
issn = "0028-3878",
publisher = "Lippincott Williams and Wilkins",
}