Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy

Richard S Finkel; Eugenio Maria Mercuri; Basil T Darras; Anne M Connolly; Nancy L Kuntz; Janbernd Kirschner; Claudia A Chiriboga; Kayoko Saito; Laurent Servais; Eduardo Tizzano; Haluk Topaloglu; Már Tulinius; Jacqueline Montes; Allan M Glanzman; Kathie Bishop; Z John Zhong; Sarah Gheuens; C Frank Bennett; Eugene Schneider; Wildon Farwell; Dominique De Vivo; C Darryl; Marco Piastra

doi:10.1056/NEJMoa1702752

Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy

Richard S Finkel^*
, Eugenio Maria Mercuri
, Basil T Darras
, Anne M Connolly
, Nancy L Kuntz
, Janbernd Kirschner
, Claudia A Chiriboga
, Kayoko Saito
, Laurent Servais
, Eduardo Tizzano
, Haluk Topaloglu
, Már Tulinius
, Jacqueline Montes
, Allan M Glanzman
, Kathie Bishop
, Z John Zhong
, Sarah Gheuens
, C Frank Bennett
, Eugene Schneider
, Wildon Farwell

Dominique De Vivo, C Darryl, Marco Piastra

^*Autore corrispondente per questo lavoro

Risultato della ricerca: Contributo in rivista › Articolo

734 Citazioni (Scopus)

Abstract

Nusinersen in spinal muscular atrophy

Lingua originale	Inglese
pagine (da-a)	1723-1732-1732
Rivista	New England Journal of Medicine
Volume	377
Numero di pubblicazione	18
DOI	https://doi.org/10.1056/NEJMoa1702752
Stato di pubblicazione	Pubblicato - 2017

All Science Journal Classification (ASJC) codes

Medicina Generale

Keywords

Age of Onset
Antisense
Artificial
Disease-Free Survival
Double-Blind Method
Female
Humans
Infant
Injections
Male
Messenger
Motor Skills
Oligonucleotides
RNA
Respiration
Spinal
Spinal Muscular Atrophies of Childhood
Survival Analysis
Survival of Motor Neuron 2 Protein

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10.1056/NEJMoa1702752

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Finkel, R. S., Mercuri, E. M., Darras, B. T., Connolly, A. M., Kuntz, N. L., Kirschner, J., Chiriboga, C. A., Saito, K., Servais, L., Tizzano, E., Topaloglu, H., Tulinius, M., Montes, J., Glanzman, A. M., Bishop, K., Zhong, Z. J., Gheuens, S., Bennett, C. F., Schneider, E., ... Piastra, M. (2017). Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy. New England Journal of Medicine, 377(18), 1723-1732-1732. https://doi.org/10.1056/NEJMoa1702752

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title = "Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy",

abstract = "Nusinersen in spinal muscular atrophy",

keywords = "Age of Onset, Antisense, Artificial, Disease-Free Survival, Double-Blind Method, Female, Humans, Infant, Injections, Male, Messenger, Motor Skills, Oligonucleotides, RNA, Respiration, Spinal, Spinal Muscular Atrophies of Childhood, Survival Analysis, Survival of Motor Neuron 2 Protein, Age of Onset, Antisense, Artificial, Disease-Free Survival, Double-Blind Method, Female, Humans, Infant, Injections, Male, Messenger, Motor Skills, Oligonucleotides, RNA, Respiration, Spinal, Spinal Muscular Atrophies of Childhood, Survival Analysis, Survival of Motor Neuron 2 Protein",

author = "Finkel, \{Richard S\} and Mercuri, \{Eugenio Maria\} and Darras, \{Basil T\} and Connolly, \{Anne M\} and Kuntz, \{Nancy L\} and Janbernd Kirschner and Chiriboga, \{Claudia A\} and Kayoko Saito and Laurent Servais and Eduardo Tizzano and Haluk Topaloglu and M{\'a}r Tulinius and Jacqueline Montes and Glanzman, \{Allan M\} and Kathie Bishop and Zhong, \{Z John\} and Sarah Gheuens and Bennett, \{C Frank\} and Eugene Schneider and Wildon Farwell and \{De Vivo\}, Dominique and C Darryl and Marco Piastra",

year = "2017",

doi = "10.1056/NEJMoa1702752",

language = "English",

volume = "377",

pages = "1723--1732--1732",

journal = "New England Journal of Medicine",

issn = "0028-4793",

publisher = "Massachussetts Medical Society",

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Finkel, RS, Mercuri, EM, Darras, BT, Connolly, AM, Kuntz, NL, Kirschner, J, Chiriboga, CA, Saito, K, Servais, L, Tizzano, E, Topaloglu, H, Tulinius, M, Montes, J, Glanzman, AM, Bishop, K, Zhong, ZJ, Gheuens, S, Bennett, CF, Schneider, E, Farwell, W, De Vivo, D, Darryl, C & Piastra, M 2017, 'Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy', New England Journal of Medicine, vol. 377, n. 18, pagg. 1723-1732-1732. https://doi.org/10.1056/NEJMoa1702752

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AU - Finkel, Richard S

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AU - Connolly, Anne M

AU - Kuntz, Nancy L

AU - Kirschner, Janbernd

AU - Chiriboga, Claudia A

AU - Saito, Kayoko

AU - Servais, Laurent

AU - Tizzano, Eduardo

AU - Topaloglu, Haluk

AU - Tulinius, Már

AU - Montes, Jacqueline

AU - Glanzman, Allan M

AU - Bishop, Kathie

AU - Zhong, Z John

AU - Gheuens, Sarah

AU - Bennett, C Frank

AU - Schneider, Eugene

AU - Farwell, Wildon

AU - De Vivo, Dominique

AU - Darryl, C

AU - Piastra, Marco

PY - 2017

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N2 - Nusinersen in spinal muscular atrophy

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KW - Artificial

KW - Disease-Free Survival

KW - Double-Blind Method

KW - Female

KW - Humans

KW - Infant

KW - Injections

KW - Male

KW - Messenger

KW - Motor Skills

KW - Oligonucleotides

KW - RNA

KW - Respiration

KW - Spinal

KW - Spinal Muscular Atrophies of Childhood

KW - Survival Analysis

KW - Survival of Motor Neuron 2 Protein

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KW - Antisense

KW - Artificial

KW - Disease-Free Survival

KW - Double-Blind Method

KW - Female

KW - Humans

KW - Infant

KW - Injections

KW - Male

KW - Messenger

KW - Motor Skills

KW - Oligonucleotides

KW - RNA

KW - Respiration

KW - Spinal

KW - Spinal Muscular Atrophies of Childhood

KW - Survival Analysis

KW - Survival of Motor Neuron 2 Protein

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JO - New England Journal of Medicine

JF - New England Journal of Medicine

IS - 18

ER -

Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy

Abstract

All Science Journal Classification (ASJC) codes

Keywords

Accesso al documento

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