Home treatment with intravenous enzyme replacement therapy with idursulfase for mucopolysaccharidosis type II - data from the Hunter Outcome Survey

Claudio Feliciani, Bk Burton, N Guffon, J Roberts, At Van Der Ploeg, Sa Jones

Risultato della ricerca: Contributo in rivistaArticolo in rivista

24 Citazioni (Scopus)

Abstract

To use our experience with patients in the observational database HOS - the Hunter Outcome Survey - to evaluate the feasibility of home infusions of idursulfase for patients with mucopolysaccharidosis type II (MPS II).
Lingua originaleEnglish
pagine (da-a)123-129
Numero di pagine7
RivistaMolecular Genetics and Metabolism
Volume101
DOI
Stato di pubblicazionePubblicato - 2010
Pubblicato esternamente

Keywords

  • Adolescent
  • Child
  • Child, Preschool
  • Enzyme Replacement Therapy
  • Home Care Services
  • Home Nursing
  • Humans
  • Iduronate Sulfatase
  • Infusion Pumps, Implantable
  • Infusions, Intravenous
  • Mucopolysaccharidosis II
  • Treatment Outcome

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