Home treatment with intravenous enzyme replacement therapy with idursulfase for mucopolysaccharidosis type II - data from the Hunter Outcome Survey

Bk Burton; N Guffon; J Roberts; At Van Der Ploeg; Sa Jones; Claudio Feliciani

doi:10.1016/j.ymgme.2010.06.011

Home treatment with intravenous enzyme replacement therapy with idursulfase for mucopolysaccharidosis type II - data from the Hunter Outcome Survey

Bk Burton, N Guffon, J Roberts, At Van Der Ploeg, Sa Jones, Claudio Feliciani

Risultato della ricerca: Contributo in rivista › Articolo in rivista

24 Citazioni (Scopus)

Abstract

To use our experience with patients in the observational database HOS - the Hunter Outcome Survey - to evaluate the feasibility of home infusions of idursulfase for patients with mucopolysaccharidosis type II (MPS II).

Lingua originale	English
pagine (da-a)	123-129
Numero di pagine	7
Rivista	Molecular Genetics and Metabolism
Volume	101
DOI	https://doi.org/10.1016/j.ymgme.2010.06.011
Stato di pubblicazione	Pubblicato - 2010
Pubblicato esternamente	Sì

Keywords

Adolescent
Child
Child, Preschool
Enzyme Replacement Therapy
Home Care Services
Home Nursing
Humans
Iduronate Sulfatase
Infusion Pumps, Implantable
Infusions, Intravenous
Mucopolysaccharidosis II
Treatment Outcome

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10.1016/j.ymgme.2010.06.011

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title = "Home treatment with intravenous enzyme replacement therapy with idursulfase for mucopolysaccharidosis type II - data from the Hunter Outcome Survey",

abstract = "To use our experience with patients in the observational database HOS - the Hunter Outcome Survey - to evaluate the feasibility of home infusions of idursulfase for patients with mucopolysaccharidosis type II (MPS II).",

keywords = "Adolescent, Child, Child, Preschool, Enzyme Replacement Therapy, Home Care Services, Home Nursing, Humans, Iduronate Sulfatase, Infusion Pumps, Implantable, Infusions, Intravenous, Mucopolysaccharidosis II, Treatment Outcome, Adolescent, Child, Child, Preschool, Enzyme Replacement Therapy, Home Care Services, Home Nursing, Humans, Iduronate Sulfatase, Infusion Pumps, Implantable, Infusions, Intravenous, Mucopolysaccharidosis II, Treatment Outcome",

author = "Bk Burton and N Guffon and J Roberts and {Van Der Ploeg}, At and Sa Jones and Claudio Feliciani",

year = "2010",

doi = "10.1016/j.ymgme.2010.06.011",

language = "English",

volume = "101",

pages = "123--129",

journal = "Molecular Genetics and Metabolism",

issn = "1096-7206",

publisher = "Academic Press Inc.",

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T1 - Home treatment with intravenous enzyme replacement therapy with idursulfase for mucopolysaccharidosis type II - data from the Hunter Outcome Survey

AU - Burton, Bk

AU - Guffon, N

AU - Roberts, J

AU - Van Der Ploeg, At

AU - Jones, Sa

AU - Feliciani, Claudio

PY - 2010

Y1 - 2010

N2 - To use our experience with patients in the observational database HOS - the Hunter Outcome Survey - to evaluate the feasibility of home infusions of idursulfase for patients with mucopolysaccharidosis type II (MPS II).

AB - To use our experience with patients in the observational database HOS - the Hunter Outcome Survey - to evaluate the feasibility of home infusions of idursulfase for patients with mucopolysaccharidosis type II (MPS II).

KW - Adolescent

KW - Child

KW - Child, Preschool

KW - Enzyme Replacement Therapy

KW - Home Care Services

KW - Home Nursing

KW - Humans

KW - Iduronate Sulfatase

KW - Infusion Pumps, Implantable

KW - Infusions, Intravenous

KW - Mucopolysaccharidosis II

KW - Treatment Outcome

KW - Adolescent

KW - Child

KW - Child, Preschool

KW - Enzyme Replacement Therapy

KW - Home Care Services

KW - Home Nursing

KW - Humans

KW - Iduronate Sulfatase

KW - Infusion Pumps, Implantable

KW - Infusions, Intravenous

KW - Mucopolysaccharidosis II

KW - Treatment Outcome

UR - http://hdl.handle.net/10807/7258

U2 - 10.1016/j.ymgme.2010.06.011

DO - 10.1016/j.ymgme.2010.06.011

M3 - Article

SN - 1096-7206

VL - 101

SP - 123

EP - 129

JO - Molecular Genetics and Metabolism

JF - Molecular Genetics and Metabolism

ER -

Home treatment with intravenous enzyme replacement therapy with idursulfase for mucopolysaccharidosis type II - data from the Hunter Outcome Survey

Abstract

Keywords

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