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Deferasirox for Transfusion-Dependent Patients with Myelodysplastic Syndromes: Safety, Efficacy, and Beyond (GIMEMA MDS0306 Trial)

  • Emanuele Angelucci
  • , Valeria Santini
  • , Anna Angela Di Tucci
  • , Giulia Quaresmini
  • , Carlo Finelli
  • , Antonio Volpe
  • , Giovanni Quarta
  • , Flavia Rivellini
  • , Grazia Sanpaolo
  • , Daniela Cilloni
  • , Flavia Salvi
  • , Giovanni Caocci
  • , Alfredo Molteni
  • , Daniele Vallisa
  • , Maria Teresa Voso
  • , Susanna Fenu
  • , Lorenza Borin
  • , Giancarlo Latte
  • , Giuliana Alimena
  • , Sergio Storti
  • Alfonso Piciocchi, Paola Fazi, Marco Vignetti, Sante Tura
  • AO Brotzu
  • University of Florence
  • Division of Infectious Diseases, Azienda Ospedaliera Papa Giovanni XXIII
  • Alma Mater Studiorum University of Bologna
  • Azienda Ospedaliera S.G. Moscati
  • Ospedale A. Perrino
  • U.O. Medicina Interna e Onco-Ematologica P.O. Umberto I
  • IRCCS Ospedale Casa Sollievo della Sofferenza - San Giovanni Rotondo (FG)
  • University of Turin
  • Division of Hematology, A.O. Nazionale Santi Antonio e Biagio e C. Arrigo
  • ATS Sardegna - ASSL Cagliari
  • Asst Grande Ospedale Metropolitano Niguarda
  • Division of Medical Oncology and Hematology, Hospital of Piacenza
  • Azienda Sanitaria Ospedaliera Molinette San Giovanni Battista Di Torino
  • Hematology University Division
  • ATS Sardegna - ASSL Nuoro
  • University of Rome La Sapienza
  • GIMEMA Foundation
  • University of Bologna

Risultato della ricerca: Contributo in rivista › Articolo › peer review

Abstract

In the absence of randomized, controlled trial data to support iron chelation therapy in transfusion-dependent patients with myelodysplastic syndromes (MDS), continued evidence from large prospective clinical trials evaluating the efficacy and safety of iron chelation therapy in this patient population is warranted.
Lingua originaleInglese
pagine (da-a)N/A-N/A
RivistaEuropean Journal of Haematology
DOI
Stato di pubblicazionePubblicato - 2014

Keywords

  • Chelation Therapy
  • Deferasirox (DFX)
  • Iron Chelation
  • Iron Overload
  • Myelodysplastic Syndromes
  • Safety
  • Serum Ferritin

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