Can the CHOP-INTEND be used as An Outcome Measure in the First Months of Age? Implications for Clinical Trials and Real World Data

Costanza Cutrona; Roberto De Sanctis; Giorgia Coratti; Anna Capasso; Martina Ricci; Giulia Stanca; Sara Carnicella; Meric Utlulig; Giulia Bersani; Ilaria Lazzareschi; Chiara Leoni; Danilo Buonsenso; Rita Paola Maria Luciano; Giovanni Vento; Richard S. Finkel; Marika Pane; Eugenio Maria Mercuri

doi:10.3233/JND-221644

Can the CHOP-INTEND be used as An Outcome Measure in the First Months of Age? Implications for Clinical Trials and Real World Data

Costanza Cutrona, Roberto De Sanctis, Giorgia Coratti, Anna Capasso, Martina Ricci, Giulia Stanca, Sara Carnicella, Meric Utlulig, Giulia Bersani, Ilaria Lazzareschi, Chiara Leoni, Danilo Buonsenso, Rita Paola Maria Luciano, Giovanni Vento, Richard S. Finkel, Marika Pane, Eugenio Maria Mercuri

St. Jude Children Research Hospital

Risultato della ricerca: Contributo in rivista › Articolo in rivista › peer review

Lingua originale	English
pagine (da-a)	85-90
Numero di pagine	6
Rivista	Journal of Neuromuscular Diseases
Volume	11
DOI	https://doi.org/10.3233/JND-221644
Stato di pubblicazione	Pubblicato - 2024

Keywords

CHOP-INTEND
SMA
early treatment
maturation
motor function
outcome measure

Accesso al documento

10.3233/JND-221644

Altri file e collegamenti

Link a IRIS PubliCatt

Cita questo

Cutrona, C., De Sanctis, R., Coratti, G., Capasso, A., Ricci, M., Stanca, G., Carnicella, S., Utlulig, M., Bersani, G., Lazzareschi, I., Leoni, C., Buonsenso, D., Luciano, R. P. M., Vento, G., Finkel, R. S., Pane, M., & Mercuri, E. M. (2024). Can the CHOP-INTEND be used as An Outcome Measure in the First Months of Age? Implications for Clinical Trials and Real World Data. Journal of Neuromuscular Diseases, 11, 85-90. https://doi.org/10.3233/JND-221644

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title = "Can the CHOP-INTEND be used as An Outcome Measure in the First Months of Age? Implications for Clinical Trials and Real World Data",

keywords = "CHOP-INTEND, SMA, early treatment, maturation, motor function, outcome measure, CHOP-INTEND, SMA, early treatment, maturation, motor function, outcome measure",

author = "Costanza Cutrona and {De Sanctis}, Roberto and Giorgia Coratti and Anna Capasso and Martina Ricci and Giulia Stanca and Sara Carnicella and Meric Utlulig and Giulia Bersani and Ilaria Lazzareschi and Chiara Leoni and Danilo Buonsenso and Luciano, {Rita Paola Maria} and Giovanni Vento and Finkel, {Richard S.} and Marika Pane and Mercuri, {Eugenio Maria}",

year = "2024",

doi = "10.3233/JND-221644",

language = "English",

volume = "11",

pages = "85--90",

journal = "Journal of Neuromuscular Diseases",

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Cutrona, C, De Sanctis, R, Coratti, G, Capasso, A, Ricci, M, Stanca, G, Carnicella, S, Utlulig, M, Bersani, G, Lazzareschi, I, Leoni, C, Buonsenso, D, Luciano, RPM, Vento, G, Finkel, RS, Pane, M & Mercuri, EM 2024, 'Can the CHOP-INTEND be used as An Outcome Measure in the First Months of Age? Implications for Clinical Trials and Real World Data', Journal of Neuromuscular Diseases, vol. 11, pagg. 85-90. https://doi.org/10.3233/JND-221644

TY - JOUR

T1 - Can the CHOP-INTEND be used as An Outcome Measure in the First Months of Age? Implications for Clinical Trials and Real World Data

AU - Cutrona, Costanza

AU - De Sanctis, Roberto

AU - Coratti, Giorgia

AU - Capasso, Anna

AU - Ricci, Martina

AU - Stanca, Giulia

AU - Carnicella, Sara

AU - Utlulig, Meric

AU - Bersani, Giulia

AU - Lazzareschi, Ilaria

AU - Leoni, Chiara

AU - Buonsenso, Danilo

AU - Luciano, Rita Paola Maria

AU - Vento, Giovanni

AU - Finkel, Richard S.

AU - Pane, Marika

AU - Mercuri, Eugenio Maria

PY - 2024

Y1 - 2024

KW - CHOP-INTEND

KW - SMA

KW - early treatment

KW - maturation

KW - motor function

KW - outcome measure

KW - CHOP-INTEND

KW - SMA

KW - early treatment

KW - maturation

KW - motor function

KW - outcome measure

UR - http://hdl.handle.net/10807/259969

U2 - 10.3233/JND-221644

DO - 10.3233/JND-221644

M3 - Article

SN - 2214-3599

VL - 11

SP - 85

EP - 90

JO - Journal of Neuromuscular Diseases

JF - Journal of Neuromuscular Diseases

ER -