@article{ef314a6fed624d048da2e4179ffcd1ae,
title = "209th ENMC International Workshop: Outcome Measures and Clinical Trial Readiness in Spinal Muscular Atrophy 7-9 November 2014, Heemskerk, The Netherlands",
abstract = "not available",
keywords = "inglese, inglese",
author = "R Finkel and Bertini, \{Enrico Silvio\} and F Muntoni and Mercuri, \{Eugenio Maria\} and K Chen and J Kirschner and \{De Lemus\}, M and Jy Hogrel and O Khwaja and M Main and E Mazzone and J Montes and D Ramsey and T Sejersen and C Sumner and K Swoboda and Tiziano, \{Francesco Danilo\} and B Tseng and \{Van Der Pol\}, L and C Villerot and B Wirth and A Witchen and Ws Yeh and A. Zittersteijn",
year = "2015",
doi = "10.1016/j.nmd.2015.04.009",
language = "English",
volume = "25",
pages = "593--602",
journal = "Neuromuscular Disorders",
issn = "0960-8966",
publisher = "Elsevier Ltd",
number = "7",
}