Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

Eugenio Maria Mercuri, Juan J Vilchez, Odile Boespflug-Tanguy, Craig M Zaidman, Jean K Mah, Nathalie Goemans, Wolfgang Müller-Felber, Erik H Niks, Ulrike Schara-Schmidt, Enrico Bertini, Giacomo P Comi, Katherine D Mathews, Laurent Servais, Krista Vandenborne, Jessika Johannsen, Sonia Messina, Stefan Spinty, Laura Mcadam, Kathryn Selby, Barry ByrneChamindra G Laverty, Kevin Carroll, Giulia Zardi, Sara Cazzaniga, Nicoletta Coceani, Paolo Bettica, Craig M Mcdonald

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)393-404
Number of pages12
JournalLANCET NEUROLOGY
Volume23
DOIs
Publication statusPublished - 2024

Keywords

  • duchenne muscular dystrophy

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