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Nusinersen efficacy data for 24-month in type 2 and 3 spinal muscular atrophy

  • Marika Pane
  • , Giorgia Coratti
  • , Maria Carmela Pera
  • , Valeria A Sansone
  • , Sonia Messina
  • , Adele d'Amico
  • , Claudio Bruno
  • , Francesca Salmin
  • , Emilio Albamonte
  • , Roberto De Sanctis
  • , Maria Sframeli
  • , Vincenzo Di Bella
  • , Simone Morando
  • , Concetta Palermo
  • , Anna Lia Frongia
  • , Laura Antonaci
  • , Anna Capasso
  • , Michela Catteruccia
  • , Antonella Longo
  • , Martina Ricci
  • Costanza Cutrona, Alice Pirola, Chiara Bravetti, Marina Pedemonte, Noemi Brolatti, Enrico Bertini, Eugenio Maria Mercuri*
*Corresponding author
  • University of Messina
  • IRCCS Ospedale pediatrico Bambino Gesù - Roma
  • IRCCS Istituto Giannina Gaslini - Genova
  • University of Milan

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Pharmacology, Toxicology and Pharmaceutical Science