Deletion of murine smn exon 7 directed to skeletal muscle leads to severe muscular dystrophy

C Cifuentes Diaz, T Frugier, Francesco Danilo Tiziano, E Lacene, N Roblot, V Joshi, M Moreau, J. Melki

Research output: Contribution to journalArticle

172 Citations (Scopus)
Original languageEnglish
Pages (from-to)1107-1114
Number of pages8
JournalTHE JOURNAL OF CELL BIOLOGY
Publication statusPublished - 2001

Keywords

  • mouse model
  • sma
  • smn

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